From Lab to Life: How a Global Conference Accelerated the Fight Against Disease

The 10th Anniversary International Drug Discovery Science and Technology Conference brought together 400+ scientists to transform research into life-saving medicines

November 8-10, 2012 Nanjing, China 400+ Participants

The Global Gathering That Shapes Medicines of Tomorrow

In November 2012, something extraordinary happened in the historic city of Nanjing, China. More than 400 brilliant minds from across the planet converged at the Nanjing International Expo Centre with a single ambitious mission: to accelerate the transformation of scientific discoveries into life-saving medicines 1 .

400+

Scientists & Researchers

19

Thematic Sessions

10th

Anniversary Edition

This conference arrived at a pivotal moment in pharmaceutical research. The first decade of the millennium had been tumultuous for drug discovery scientists, with many large pharmaceutical companies withdrawing from research areas including central nervous system disorders, hypertension, and other complex diseases 3 . Yet simultaneously, a renaissance was emerging as excellent scientists moved into academic drug discovery centers, virtual companies, and research foundations 3 .

The Science Spectrum: From Cancer to Orphan Diseases

A Conference Within Many Conferences

The scale and diversity of the 2012 IDDST was staggering—19 separate thematic chapters ran simultaneously across multiple parallel sessions, creating essentially "many conferences under one roof" 1 .

Session Category Specific Topics Covered
Discovery Biology Target validation, pharmacology and toxicology, stem cells and regenerative medicine
Chemical Technologies Chemistry, rational drug design, drug screening technology, bioprocessing
Analytical Approaches 'Omics' technologies, analytical, automation and enabling technologies, informatics
Disease Focus Areas Cancer, CNS disorders, respiratory and inflammation, autoimmune diseases, emerging infectious diseases, bone diseases, orphan diseases
Special Programs Bench to Bedside to Business, Chinese Scientist programme
Neurodegeneration Focus

The 6th Drug Discovery for Neurodegeneration Conference emphasized the growing recognition of these disorders as "one of the greatest unmet health needs" 2 .

Integrated Approaches

Researchers discussed moving beyond single-target strategies to combine them with functional approaches—a methodological evolution in pharmacological thinking 2 .

A Closer Look: VAL-083 and the Rebirth of a Cancer Drug

The Experiment That Gave Old Drugs New Life

One of the most compelling presentations at the conference came from Jeffrey Bacha, CEO of Del Mar Pharmaceuticals, who showcased the remarkable journey of VAL-083—a chemotherapeutic agent with a complex history now being "repositioned" for glioblastoma multiforme (GBM), the most common and aggressive form of brain cancer 5 .

VAL-083, known as "DAG for Injection" in China, was already approved there for chronic myelogenous leukemia (CML) and lung cancer 5 . Its story illustrates an increasingly important pathway in drug development: finding new applications for existing medications.

Drug Repositioning

Finding new therapeutic applications for existing drugs can significantly accelerate development timelines and reduce costs.

Methodology: Designing a Smarter Attack on Brain Cancer

Mechanism Investigation

Confirmed VAL-083's unique action as a bi-functional alkylating agent

Resistance Testing

Tested against cancer cells resistant to standard therapies

Dosing Optimization

Developed new regimens for modern brain cancer protocols

Collaborative Validation

Partnership between Del Mar and Guangxi Wuzhou Pharmaceuticals

VAL-083's Multidimensional Activity Profile
Cancer Type Resistance Mechanism Overcome Development Status
Glioblastoma Multiforme MGMT repair enzyme-mediated resistance Phase I/II clinical trials
Chronic Myelogenous Leukemia Tyrosine kinase inhibitor (TKI) resistance Approved in China, expanded use under investigation
Lung Cancer Tyrosine kinase inhibitor (TKI) resistance Approved in China, expanded use under investigation
Clinical Development Timeline
Historical

NCI-sponsored research

Activity against various tumor types suggested potential beyond original indications

Pre-2012

Chinese approval

Approved for CML and lung cancer as "DAG for Injection"

2011

AACR presentation

Data showed activity against therapy-resistant GBM cell lines

2012

IDDST presentation

Broader resistance-overcoming profile revealed, clinical trial designs presented

Post-2012

Phase I/II clinical trials

Ongoing evaluation for safety, tolerability and anti-tumor activity in GBM patients

The Scientist's Toolkit: Essential Technologies Driving Discovery

Biomimetic Chromatography

Tools that mimic biological membranes to predict how potential drugs will behave in living systems, highlighted by Professor Klara Valko's work on physicochemical characterization 8 .

High-Throughput Screening

Automated systems that can rapidly test thousands of compounds against biological targets, mentioned as essential capabilities in emerging academic drug discovery centers 3 .

'Omics' Technologies

Comprehensive analysis tools (genomics, proteomics, metabolomics) that allow scientists to understand disease at a systems level rather than through single targets 1 .

Stem Cell Tools

Technologies that create more human-relevant disease models for testing potential therapies, noted as a dedicated session topic at the conference 1 .

Technology Adoption in Drug Discovery

High-Throughput Screening 85%
Omics Technologies 78%
Stem Cell Models 65%
PBPK Modeling 72%

Collaboration as Catalyst: When Academia Meets Industry

Breaking Down the Ivory Towers

A recurring theme throughout the conference was the growing importance of collaboration between academic research centers and pharmaceutical companies. As one editorial noted, "Many excellent scientists are now engaged in new venues that include virtual companies, research foundations, and academic drug discovery centers" 3 .

"Drug discovery in the pharmaceutical industry is and will remain a research-based endeavor. Everyone recognizes that there is no guarantee of success... More importantly, even with a solid translational foundation, there is no clear path to improving the number of candidates that progress from discovery through the clinic, regardless of the criteria used to vet and evaluate programs" 3 .

Academic Drug Discovery Centers
  • Vanderbilt University Established
  • University of Pittsburgh Established
  • University of North Carolina Established
  • Yale University Established
  • University of Kansas Established

The Chinese Context: A Rising Power in Pharmaceutical Research

The conference's location in Nanjing highlighted China's rapidly expanding role in global drug discovery. The collaboration between Del Mar Pharmaceuticals and Guangxi Wuzhou Pharmaceuticals exemplified this trend, combining Western research with Chinese manufacturing and clinical experience 5 .

Similarly, Chinese scientists like Professor Ao Zhang—who returned to China after positions at Harvard Medical School and McLean Hospital—represented the reverse "brain drain" that was strengthening China's research capabilities 8 .

Reverse Brain Drain

Chinese scientists returning from positions abroad are strengthening domestic research capabilities

Beyond 2012: The Lasting Impact of a Scientific Gathering

From Nanjing to the World

The 10th Anniversary IDDST conference generated momentum that extended far beyond its three-day schedule. The collaborations initiated, ideas cross-pollinated, and partnerships formed in Nanjing continued to influence drug discovery science for years afterward.

Drug Repositioning Innovation

The VAL-083 story inspired similar approaches for other existing drugs, potentially accelerating development timelines.

International Networks

Connections formed between Chinese, European, and North American researchers fostered ongoing collaborations.

Educational Impact

The influx of industrial scientists into academic settings helped train a new generation of researchers.

The Unfinished Journey

Despite the exciting progress showcased at IDDST 2012, presenters and attendees recognized that many challenges remained. The "valley of death" between basic research and approved medicines still claimed many promising compounds. The high cost of drug development continued to limit investment in some disease areas. And the need for better predictive models—especially for complex conditions like neurodegenerative diseases—remained largely unfulfilled 2 3 .

Yet the 2012 IDDST conference embodied a growing determination within the scientific community to confront these challenges collectively, innovatively, and with an expanding toolkit of technologies and strategies. As the conference series prepares for its 21st annual meeting in Stockholm in 2025, the legacy of those November days in Nanjing continues through each new collaboration formed, each promising compound discovered, and each life potentially improved through the dedicated work of drug discovery scientists worldwide 4 .

References

References