Explore how advanced therapy medicinal products (ATMPs) are revolutionizing medicine while challenging traditional regulatory frameworks.
How scientists are engineering microscopic particles to deliver healing cargo directly to diseased cells
Explore how systemic, tumor-targeted p53 gene therapy is revolutionizing cancer treatment by reawakening the body's natural defense mechanisms.
Discover how bone marrow transplantation is revolutionizing hemophilia A treatment through groundbreaking mouse studies showing cellular correction of Factor VIII deficiency.
Breakthrough gene therapy fidanacogene elaparvovec shows long-term efficacy in treating hemophilia B with a single dose, potentially curing this genetic bleeding disorder.